Phase I clinical trial results of aceneuramic acid for GNE myopathy in Japan
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Publisher
Springer Science and Business Media LLC
Link
http://link.springer.com/content/pdf/10.1186/s41231-018-0025-0.pdf
Reference37 articles.
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1. Efficacy confirmation study of aceneuramic acid administration for GNE myopathy in Japan;Orphanet Journal of Rare Diseases;2023-08-11
2. Phase II/III Study of Aceneuramic Acid Administration for GNE Myopathy in Japan;Journal of Neuromuscular Diseases;2023-07-04
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