Regression of left ventricular hypertrophy after tafamidis therapy in a patient with transthyretin amyloidosis variant

Author:

Yagi Shusuke1,Yamazaki Hiromu1,Kusunose Kenya1,Osaki Yusuke2,Ise Takayuki1,Kadota Muneyuki1,Tserensonom Munkhtsetseg1,Kawabata Yutaka1,Hara Tomoya1,Ueno Rie1,Saijo Yoshihito1,Matsuura Tomomi1,Yamaguchi Koji1,Yamada Hirotsugu1,Fukuda Daiju1,Soeki Takeshi1,Wakatsuki Tetsuzo1,Sata Masataka1

Affiliation:

1. Department of Cardiovascular Medicine, Tokushima University Graduate School of Biomedical Sciences, Tokushima, Japan

2. Department of Neurology, Tokushima University Graduate School of Biomedical Sciences, Tokushima, Japan

Publisher

University of Tokushima Faculty of Medicine

Subject

General Biochemistry, Genetics and Molecular Biology,General Medicine

Reference5 articles.

1. 1. Coelho T, Maia LF, Martins da Silva A, Waddington Cruz M, Planté-Bordeneuve V, Lozeron P, Suhr OB, Campistol JM, Conceição IM, Schmidt HH-J, Trigo P, Kelly JW, Labaudinière R, Chan J, Packman J, Wilson A, Grogan DR : Tafamidis for transthyretin familial amyloid polyneuropathy : a randomized, controlled trial. Neurology 79 : 785-92, 2012

2. 2. Maurer MS, Schwartz JH, Gundapaneni B, Elliott PM, Merlini G, Waddington-Cruz M, Kristen AV, Grogan M, Witteles R, Damy T, Drachman BM, Shah SJ, Hanna M, Judge DP, Barsdorf AI, Huber P, Patterson TA, Riley S, Schumacher J, Stewart M, Sultan MB, Rapezzi C : Tafamidis Treatment for Patients with Transthyretin Amyloid Cardiomyopathy. N Engl J Med 379 : 1007-1016, 2018

3. 3. Endo J, Sano M, Izumiya Y, Tsujita K, Nakamura K, Tahara N, Kuwahara K, Inomata T, Ueda M, Sekijima Y, Ando Y, Tsutsui H, Isobe M, Fukuda K : A Statement on the Appropriate Administration of Tafamidis in Patients With Transthyretin Cardiac Amyloidosis. Circ J 84 : 15-17, 2019

4. 4. Brahmanandam V, McGraw S, Mirza O, Desai AA, Farzaneh-Far A : Regression of Cardiac Amyloidosis After Stem Cell Transplantation Assessed by Cardiovascular Magnetic Resonance Imaging. Circulation 129 : 2326-2328, 2014

5. 5. Damy T, Judge DP, Kristen AV, Berthet K, Li H, Aarts J : Cardiac Findings and Events Observed in an Open-Label Clinical Trial of Tafamidis in Patients with non-Val30Met and non-Val122Ile Hereditary Transthyretin Amyloidosis. J Cardiovasc Transl Res 8 : 117-127, 2015

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