1. United States Food and Drug Administration. FDA approval brings first gene therapy to the United States, https://www.fda.gov/news-events/press-announcements/fda-approval-brings-first-gene-therapy-united-states [accessed 20.05.20].
2. United States Food and Drug Administration. FDA approves axicabtagene ciloleucel for large B-cell lymphoma, https://www.fda.gov/drugs/resources-information-approved-drugs/fda-approves-axicabtagene-ciloleucel-large-b-cell-lymphoma [accessed 20.05.20].
3. Transfusion independence and HMGA2 activation after gene therapy of human beta-thalassaemia;Cavazzana-Calvo;Nature,2010
4. Gene therapy in a patient with sickle cell disease;Ribeil;N Engl J Med,2017
5. Gene therapy as a curative option for beta-thalassemia;Biffi;N Engl J Med,2018