Efficacy, safety, and pharmacokinetics of a new, ready-to-use, liquid hydroxyurea in children with sickle cell anemia

Author:

Rankine-Mullings Angela1,Keenan Russell2,Chakravorty Subarna3ORCID,Inusa Baba4ORCID,Telfer Paul5,Velangi Mark6,Ware Russell E.7ORCID,Moss Jon J.8,Lloyd Adam L.8,Edwards Sarah9,Mulla Hussain9ORCID

Affiliation:

1. 1Sickle Cell Unit, Caribbean Institute for Health Research, The University of The West Indies, Mona, Jamaica

2. 2Liverpool Paediatric Haemophilia Centre, Haematology Treatment Centre, Alder Hey Children’s Hospital, NHS Foundation Trust, Liverpool, United Kingdom

3. 3Department of Paediatric Haematology, Kings College Hospital, NHS Foundation Trust, London, United Kingdom

4. 4Department of Paediatric Haematology, Evelina London Children’s Hospital, Guy’s and St. Thomas NHS Foundation Trust, London, United Kingdom

5. 5Department of Paediatric Haematology, Royal London Hospital, Barts Health NHS Trust, London, United Kingdom

6. 6Department of Paediatric Haematology, Birmingham Children’s Hospital NHS Foundation Trust, Birmingham, United Kingdom

7. 7Division of Hematology and Global Health Center, Cincinnati Children’s Hospital, Cincinnati, OH

8. 8Bast Inc Limited, Leicester, United Kingdom

9. 9Nova Laboratories Limited, Leicester, United Kingdom

Publisher

American Society of Hematology

Subject

Hematology

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