1. Department of Pathology and Laboratory Medicine and
2. Gene Therapy Center, University of North Carolina at Chapel Hill, Chapel Hill, NC;
3. Center for Inherited Blood Disorders, Orange, CA;
4. Division of Pediatric Hematology/Oncology, Department of Pediatrics, University of California, Los Angeles, CA;
5. Anschutz Medical Campus, University of Colorado Denver, Aurora, CO; and
6. Division of Blood Disorders, National Center on Birth Defects and Developmental Disabilities, Centers for Disease Control and Prevention, Atlanta, GA