HLA-haploidentical stem cell transplantation after removal of αβ+ T and B cells in children with nonmalignant disorders

Author:

Bertaina Alice1,Merli Pietro1,Rutella Sergio12,Pagliara Daria1,Bernardo Maria Ester1,Masetti Riccardo3,Pende Daniela4,Falco Michela5,Handgretinger Rupert6,Moretta Francesca1,Lucarelli Barbarella1,Brescia Letizia P.1,Li Pira Giuseppina1,Testi Manuela7,Cancrini Caterina8,Kabbara Nabil9,Carsetti Rita1,Finocchi Andrea8,Moretta Alessandro10,Moretta Lorenzo5,Locatelli Franco111

Affiliation:

1. Department of Pediatric Hematology and Oncology, Istituto di Ricovero e Cura a Carattere Scientifico Bambino Gesù Children’s Hospital, Rome, Italy;

2. Department of Medical Sciences, Catholic University Medical School, Rome, Italy;

3. Department of Pediatrics, Sant’Orsola Hospital, University of Bologna, Bologna, Italy;

4. Istituto di Ricovero e Cura a Carattere Scientifico Azienda Ospedaliera Universitaria San Martino-Istituto Nazionale per la Ricerca sul Cancro, Genoa, Italy;

5. Istituto di Ricovero e Cura a Carattere Scientifico Giannina Gaslini, Genoa, Italy;

6. Children’s University Hospital, University of Tuebingen, Tuebingen, Germany;

7. Laboratory of Immunogenetics and Transplant Biology, Istituto Mediterraneo di Ematologia Foundation at Tor Vergata University Hospital, Rome, Italy;

8. University Department of Pediatrics, Istituto di Ricovero e Cura a Carattere Scientifico Bambino Gesù Children’s Hospital, University of Rome Tor Vergata, Rome, Italy;

9. Pediatric Hematology Oncology Division, Rafic Hariri University Hospital, Beirut, Lebanon;

10. Dipartimento di Medicina Sperimentale and Centro di Eccellenza per la Ricerca Biomedica, Università di Genova, Genoa, Italy; and

11. Department of Pediatrics, University of Pavia, Pavia, Italy

Abstract

Key Points Removal of αβ+ T and CD19+ B cells is an effective strategy for successful HLA-haploidentical hematopoietic stem cell transplantation. The high probability of disease-free survival renders this transplant option attractive for any child with a nonmalignant disorder.

Publisher

American Society of Hematology

Subject

Cell Biology,Hematology,Immunology,Biochemistry

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