Sickle cell disease: an international survey of results of HLA-identical sibling hematopoietic stem cell transplantation

Author:

Gluckman Eliane12,Cappelli Barbara2,Bernaudin Francoise3,Labopin Myriam4,Volt Fernanda12,Carreras Jeanette5,Pinto Simões Belinda6,Ferster Alina7,Dupont Sophie8,de la Fuente Josu9,Dalle Jean-Hugues10,Zecca Marco11,Walters Mark C.12,Krishnamurti Lakshmanan13,Bhatia Monica14,Leung Kathryn15,Yanik Gregory16,Kurtzberg Joanne17,Dhedin Nathalie18,Kuentz Mathieu3,Michel Gerard19,Apperley Jane20,Lutz Patrick21,Neven Bénédicte22,Bertrand Yves23,Vannier Jean Pierre24,Ayas Mouhab25,Cavazzana Marina262728,Matthes-Martin Susanne29,Rocha Vanderson13031,Elayoubi Hanadi12,Kenzey Chantal12,Bader Peter32,Locatelli Franco3334,Ruggeri Annalisa1235,Eapen Mary5

Affiliation:

1. Eurocord, Paris-Diderot University Equipe d'Accueil 3518, Hospital Saint Louis, Paris, France;

2. Monacord, International Observatory on Sickle Cell Disease, Centre Scientifique de Monaco, Monaco;

3. Department of Pediatrics, Referral Center for Sickle Cell Disease, Centre Hospitalier Intercommunal Créteil, Paris XII University, Créteil, France;

4. European Society for Blood and Marrow Transplantation Statistical Unit, Hospital Saint Antoine, Assistance Publique-Hôpitaux de Paris, Paris, France;

5. Department of Medicine, Center for International Blood and Marrow Transplant Research, Medical College of Wisconsin, Milwaukee, WI;

6. Ribeirão Preto Medical School, University of São Paulo, São Paulo, Brazil;

7. Hemato-Oncology Unit, Hospital Universitaire des Enfants Reine Fabiola, Université Libre de Bruxelles, Brussels, Belgium;

8. Cliniques Universitaires Saint Luc, Hemato-Oncology Unit, Brussels, Belgium;

9. Centre for Haematology, Imperial College London, London, United Kingdom;

10. Hemato-immunology, Hospital Robert Debré and Paris-Diderot University, Paris, France;

11. Pediatric Hematology-Oncology, Fondazione Istituto di Ricovero e Cura a Carattere Scientifico Policlinico San Matteo, Pavia, Italy;

12. University of California San Francisco Benioff Children's Hospital, Oakland, CA;

13. Aflac Cancer and Blood Disorders Center, Children's Healthcare of Atlanta, Atlanta, GA;

14. Morgan Stanley Children’s Hospital of New York, New York, NY;

15. Baylor College of Medicine, Houston, TX;

16. Children’s Hospital of Michigan, Detroit, MI;

17. Pediatric Blood and Marrow Transplant Program, Duke University Medical Center, Durham, NC;

18. Adolescent and Young Adults Hematology Department, Hospital Saint-Louis, Paris, France;

19. Department of Pediatric Hematology and Oncology and Research Unit Equipe d'Accueil 3279, Aix-Marseille University and Timone Children's Hospital Marseille, Marseille, France;

20. Imperial College London, Hammersmith Hospital, London, United Kingdom;

21. Service D'hémato Oncologie Pédiatrique, Centre Hospitalier Universitaire de Strasbourg, Strasbourg, France;

22. Pediatric Hematology-Immunology Department, Hospital Necker-Enfants Malades, Assistance Publique–Hôpitaux de Paris, Paris, France;

23. Department of Pediatric Hematology and Oncology, University Hospital of Lyon, Lyon, France;

24. Equipe d'Accueil 3829, Institut de Recherche et d'Innovation Biomédicale, Faculté de Médecine-Pharmacie, Rouen, France;

25. Paediatric Haematology/Oncology, King Faisal Specialist Hospital & Research Centre, Riyadh, Saudi Arabia;

26. Biotherapy Department, Necker Children’s Hospital, Assistance Publique-Hôpitaux de Paris, Paris, France;

27. Biotherapy Clinical Investigation Center, Groupe Hospitalier Universitaire Ouest, Assistance Publique-Hôpitaux de Paris, INSERM, Paris, France;

28. Paris Descartes–Sorbonne Paris Cité University, Imagine Institute, Paris, France;

29. Stem Cell Transplantation Unit, St. Anna Children's Hospital, Vienna, Austria;

30. Hospital Sirio-Libanes, and Serviço de Hematologia, Hemoterapia e Terapia Celular, São Paulo University, São Paulo, Brazil;

31. Churchill Hospital, Oxford, United Kingdom;

32. Department for Stem Cell Transplantation and Immunology, Clinic for Children and Adolescents, University Hospital Frankfurt, Goethe University, Frankfurt, Germany;

33. Dipartimento di Oncoematologia Pediatrica, Istituto di Ricovero e Cura a Carattere Scientifico, Ospedale Bambino Gesù, Rome, Italy;

34. Dipartimento di Scienze Pediatriche, Università di Pavia, Pavia, Italy; and

35. Department of Hematology and Cell Therapy, Hospital Saint Antoine, Paris, France

Abstract

Key Points HLA-identical sibling transplantation for SCD offers excellent long-term survival. Mortality risk is higher for older patients; event-free survival has improved in patients transplanted after 2006.

Publisher

American Society of Hematology

Subject

Cell Biology,Hematology,Immunology,Biochemistry

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