1. Centre for Immunodeficiency, Molecular Immunology Unit, UCL Institute of Child Health, London, United Kingdom;
2. Department of Blood and Marrow Transplantation, Great Ormond Street Hospital, London, United Kingdom;
3. Department of Pediatrics, University Hospital Ulm, Ulm, Germany;
4. Institute of Cellular Medicine, Newcastle University, Newcastle upon Tyne, United Kingdom;
5. Department of Pediatrics, Leiden University Medical Center, Leiden, The Netherlands;
6. University Department of Pediatrics, Children's Hospital Bambino Gesù-University of Rome Tor Vergata (DPUO), Rome, Italy;
7. San Raffaele Telethon Institute for Gene Therapy (HSR-TIGET), Milan, Italy;
8. Department of Paediatrics, University of Brescia, Brescia, Italy;
9. Bone Marrow Transplant Unit, Royal Hospital for Children, Bristol, United Kingdom;
10. Division of Bone Marrow Transplant and Immune Deficiency, Cincinnati Children's Hospital Medical Center, Cincinnati, OH;
11. Pediatric Hematology, Oncology and Stem Cell Transplantation, Ghent University Hospital, Ghent, Belgium;
12. Department of Pediatrics, College of Medicine, King Saud University, Riyadh, Saudi Arabia;
13. Department of Pediatrics, King Faisal Specialist Hospital and Research Center, Riyadh, Saudi Arabia;
14. Center for Chronic Immunodeficiency, University Medical Center Freiburg, Germany;
15. Unité d'Immuno-Hématologie et Rhumatologie Pédiatrique and French National Reference Center for Primary Immune Deficiencies (CEREDIH), Hôpital Necker-Enfants Malades, Assistance Publique–Hôpitaux de Paris (AP-HP), Paris, France;
16. Division of Oncology, Children's Hospital of Philadelphia, Philadelphia, PA;
17. Division of Allergy and Clinical Immunology, The Hospital for Sick Children, Toronto, ON;
18. Department of Pediatrics, Pediatric Blood and Marrow Transplantation Program, University Medical Center Utrecht, Utrecht, The Netherlands;
19. Department of Biotherapy, Hopital Necker-Enfants Malades; Inserm and AP-HP Clinical Investigation Center in Biotherapy; Universite Paris Descartes, Sorbonne Paris Cite, Faculté de Médecine, Paris, France; and
20. Division of Immunology and the Manton Center for Orphan Disease Research, Children's Hospital Boston, Harvard Medical School, Boston, MA