Radiation-free, alternative-donor HCT for Fanconi anemia patients: results from a prospective multi-institutional study-Reference-Cited by-同舟云学术

Radiation-free, alternative-donor HCT for Fanconi anemia patients: results from a prospective multi-institutional study

Published:2017-04-20 Issue:16 Volume:129 Page:2308-2315
ISSN:0006-4971
Container-title:Blood
language:en
Short-container-title:

Author:

Mehta Parinda A.¹^ORCID,Davies Stella M.¹,Leemhuis Thomas¹,Myers Kasiani¹,Kernan Nancy A.²³^ORCID,Prockop Susan E.²³,Scaradavou Andromachi²³,O’Reilly Richard J.²³,Williams David A.⁴,Lehmann Leslie⁴,Guinan Eva⁵^ORCID,Margolis David⁶^ORCID,Baker K. Scott⁷,Lane Adam¹,Boulad Farid²³

Affiliation:

1. Division of Bone Marrow Transplantation and Immune Deficiency, Cincinnati Children’s Hospital Medical Center, Cincinnati, OH;

2. Department of Pediatrics, Bone Marrow Transplant Service, Memorial Sloan Kettering, New York, NY;

3. Division of Pediatric Hematology-Oncology, New York Presbyterian Hospital–Weill Cornell Medical College, New York, NY;

4. Dana-Farber/Boston Children’s Cancer and Blood Disorders Center, Harvard Medical School and Harvard Stem Cell Institute, Boston, MA;

5. Department of Radiation Oncology, Dana-Farber Cancer Institute, Boston, MA;

6. Children’s Hospital of Wisconsin, Milwaukee, WI; and

7. Fred Hutchinson Cancer Research Center, Seattle, WA

Abstract

Key Points Alternative donor HCT can be performed in patients with FA without using radiation. All 26 patients younger than 10 years of age undergoing HCT for marrow failure using lower-dose busulfan-containing regimen survived.

Publisher

American Society of Hematology

Subject

Cell Biology,Hematology,Immunology,Biochemistry

Link

http://ashpublications.org/blood/article-pdf/129/16/2308/1399702/blood743112.pdf

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