Revised response criteria for polycythemia vera and essential thrombocythemia: an ELN and IWG-MRT consensus project

Author:

Barosi Giovanni1,Mesa Ruben2,Finazzi Guido3,Harrison Claire4,Kiladjian Jean-Jacques5,Lengfelder Eva6,McMullin Mary F.7,Passamonti Francesco8,Vannucchi Alessandro M.9,Besses Carlos10,Gisslinger Heinz11,Samuelsson Jan12,Verstovsek Srdan13,Hoffman Ronald14,Pardanani Animesh15,Cervantes Francisco16,Tefferi Ayalew15,Barbui Tiziano3

Affiliation:

1. Center for the Study of Myelofibrosis, Biotechnology Research Area, Istituto di Ricovero e Cura a Carattere Scientifico Policlinico S. Matteo Foundation, Pavia, Italy;

2. Division of Hematology and Medical Oncology, Mayo Clinic, Scottsdale, AZ;

3. Division of Hematology and Research Foundation, Ospedale Papa Giovanni XXIII, Bergamo, Italy;

4. Department of Haematology, St Thomas Hospital, London, United Kingdom;

5. Saint-Louis Hospital and Paris Diderot University, Paris, France;

6. Department of Hematology and Oncology, University Hospital Mannheim, Mannheim, Germany;

7. Centre for Cancer Research and Cell Biology, Queen’s University, Belfast, United Kingdom;

8. Division of Hematology, Department of Internal Medicine, Ospedale di Circolo e Fondazione Macchi, Varese, Italy;

9. University of Florence, Florence, Italy;

10. Department of Hematology, Institut Hospital del Mar d'Investigations Mediques, Barcelona, Spain;

11. University of Vienna, Department of Internal Medicine, Wien, Austria;

12. Department of Internal Medicine, Karolinska Institute at Stockholm South Hospital, Stockholm, Sweden;

13. MD Anderson Cancer Center, Houston, TX;

14. Division of Hematology/Oncology, Pathology and Surgery, Tisch Cancer Institute, Myeloproliferative Disorders Research Consortium, Mount Sinai School of Medicine, New York, NY;

15. Division of Hematology, Department of Medicine, Mayo Clinic, Rochester, MN; and

16. University of Barcelona, Hospital Clínic, Hematology Department, Institut D’Investigacions Biomèdiques August Pi i Sunyer, Barcelona, Spain

Abstract

Key Points Evidence exists that ELN criteria for response in ET and PV issued in 2009 do not provide relevant measures of benefit for patients. Revised recommendations for assessing response are provided.

Publisher

American Society of Hematology

Subject

Cell Biology,Hematology,Immunology,Biochemistry

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