1. Wellcome Sanger Institute, Hinxton, United Kingdom;
2. Department of Haematology, University College London Hospital, London, United Kingdom;
3. Department of Haematology, University College London Cancer Institute, London, United Kingdom;
4. Cambridge University Hospitals National Health Service (NHS) Foundation Trust, Cambridge, United Kingdom;
5. Department of Haematology, University of Cambridge, Cambridge, United Kingdom;
6. Cambridge Stem Cell Institute, Cambridge, Cambridgeshire, United Kingdom;
7. Department of Medical Genetics, National Institute for Health Research Cambridge Biomedical Research Centre, University of Cambridge, Cambridge, United Kingdom;
8. University College London Great Ormond Street Institute of Child Health, London, United Kingdom;
9. Great Ormond Street Hospital for Children NHS Foundation Trust, London, United Kingdom;
10. The Hospital for Sick Children, Toronto, ON, Canada; and
11. Department of Pathology and
12. Department of Paediatrics, University of Cambridge, Cambridge, United Kingdom