CRISPR/Cas9 PIG-A gene editing in nonhuman primate model demonstrates no intrinsic clonal expansion of PNH HSPCs-Reference-Cited by-同舟云学术

CRISPR/Cas9 PIG-A gene editing in nonhuman primate model demonstrates no intrinsic clonal expansion of PNH HSPCs

Published:2019-06-06 Issue:23 Volume:133 Page:2542-2545
ISSN:0006-4971
Container-title:Blood
language:en
Short-container-title:

Author:

Shin Tae-Hoon¹^ORCID,Baek Eun Jung¹²^ORCID,Corat Marcus A. F.¹³,Chen Shirley¹,Metais Jean-Yves¹⁴,AlJanahi Aisha A.¹,Zhou Yifan¹,Donahue Robert E.¹,Yu Kyung-Rok¹⁵^ORCID,Dunbar Cynthia E.¹^ORCID

Affiliation:

1. Translational Stem Cell Biology Branch, National Heart, Lung, and Blood Institute, National Institutes of Health, Bethesda, MD;

2. Department of Laboratory Medicine, College of Medicine, Hanyang University, Seoul, Republic of Korea;

3. Multidisciplinary Center for Biological Research, University of Campinas, Campinas, Brazil;

4. Department of Bone Marrow Transplantation and Cellular Therapy, St. Jude Children’s Research Hospital, Memphis, TN; and

5. Department of Medical Life Sciences, College of Medicine, The Catholic University of Korea, Seoul, Republic of Korea

Publisher

American Society of Hematology

Subject

Cell Biology,Hematology,Immunology,Biochemistry

Link

http://ashpublications.org/blood/article-pdf/133/23/2542/1553610/bloodbld2019000800.pdf

Reference23 articles.

1. Therapeutic genome editing: prospects and challenges;Cox;Nat Med,2015

2. Gene editing of human hematopoietic stem and progenitor cells: Promise and potential hurdles;Yu;Hum Gene Ther,2016

3. Hematopoietic stem cell gene therapy: assessing the relevance of preclinical models;Larochelle;Semin Hematol,2013

4. Somatic mutations in paroxysmal nocturnal hemoglobinuria: a blessing in disguise?;Luzzatto;Cell,1997

5. Paroxysmal nocturnal hemoglobinuria;Brodsky;Blood,2014

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4. Immune pressure on hematopoietic stem cells can drastically expand glycosylphosphatidylinositol-deficient clones in paroxysmal nocturnal hemoglobinuria;2023-09-06

5. Long noncoding RNA FAM157C contributes to clonal proliferation in paroxysmal nocturnal hemoglobinuria;Annals of Hematology;2023-01-06