1. Sarepta Therapeutics, Inc., Cambridge, MA, USA
2. UPMC Children’s Hospital of Pittsburgh, Pittsburgh, PA, USA
3. University of Florida, Gainesville, FL, USA
4. Nationwide Children’s Hospital, The Ohio State University College of Medicine, Columbus, OH, USA
5. Rush University Medical Center, Chicago, IL, USA
6. Children’s Hospital of The King’s Daughters, Norfolk, VA, USA
7. University of California Los Angeles, Los Angeles, CA, USA
8. Kennedy Krieger Institute, Johns Hopkins School of Medicine, Baltimore, MD, USA
9. Analysis Group, Inc., Boston, MA, USA
10. University Hospitals Leuven, Leuven, Belgium
11. University of California Davis Health System, Sacramento, CA, USA
12. Catholic University, Rome, Italy