1. Departments of Physical Medicine & Rehabilitation and Pediatrics, University of California Davis Health System and School of Medicine, Sacramento, CA, USA
2. Department of Neurology, University of California, Los Angeles, Los Angeles, CA, USA
3. UPMC Children’s Hospital of Pittsburgh, Pittsburgh, PA, USA
4. Pediatrics, Center for Gene Therapy, Nationwide Children’s Hospital, Columbus, OH, USA
5. University of Rochester Medical Center, Rochester, NY, USA
6. Center for Genetic Muscle Disorders, Kennedy Krieger Institute, Baltimore, MD, USA
7. Departments of Neurology and Neuroscience, Johns Hopkins School of Medicine, Baltimore, MD, USA
8. Department of Pediatrics and Child Neurology, University Hospitals Leuven, Leuven, Belgium
9. Pediatric Neurology, Catholic University, Rome, Italy
10. Sarepta Therapeutics, Inc., Cambridge, MA, USA