1. Department for Human Genetics and Hussman Institute for Human Genomics, University of Miami, Miami, FL, USA
2. Department of Comparative Biosciences and Waisman Center, University of Wisconsin, Madison, WI, USA
3. Data Management and Coordinating Center, Rare Diseases Clinical Research Network, Pediatrics Epidemiology Center, University of South Florida, Tampa, FL, USA
4. Department of Neurology, University of Iowa, Iowa City, IA, USA
5. Department of Neurology, Academic Medical Centre, Amsterdam, The Netherlands
6. Department of Neurology, University of Miami, Miami, FL, USA
7. Department of Neurology, University of Rochester, Rochester, NY, USA
8. Department of Neurology, Stanford University, Palo Alto, CA, USA
9. Department of Neurology, Johns Hopkins University School of Medicine, Baltimore, MD, USA
10. Department of Neuroscience, Johns Hopkins University School of Medicine, Baltimore, MD, USA
11. Department of Neurology, Wayne State University School of Medicine, Detroit, MI, USA
12. Division of Neurology, The Children’s Hospital of Philadelphia, Philadelphia, PA, USA
13. IRCCS Foundation Carlo Besta Neurological Institute, Milan, Italy
14. Department of Clinical Genetics, Leiden University Medical Center, Leiden, The Netherlands
15. Department of Neurology, Samsung Medical Center, Sungkyunkwan University School of Medicine, Seoul, Korea
16. Department of Neurology, Perelman School of Medicine, University of Pennsylvania, Philadelphia, PA, USA
17. MRC Centre for Neuromuscular Diseases, UCL Institute of Neurology, Queen Square, London, UK