Safety Monitoring of Gene Therapy for Spinal Muscular Atrophy with Onasemnogene Abeparvovec –A Single Centre Experience
Author:
Affiliation:
1. Department of Neuropediatrics, University Hospital Bonn, Bonn, Germany
2. Department of Pediatric Cardiology, University Hospital Bonn, Bonn, Germany
Abstract
Publisher
IOS Press
Subject
Clinical Neurology,Neurology
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