1. Cure SMA, Elk Grove Village, IL, USA
2. Stanford University, Stanford, CA, USA
3. Muscular Dystrophy Association, Chicago, IL, USA
4. Washington University School of Medicine, St. Louis, MO, USA
5. Department of Neurology, Boston Children’s Hospital, Boston, MA, USA
6. Nemours Children’s Hospital, University of Central Florida College of Medicine, Orlando, FL, USA
7. Miller School of Medicine, University of Miami, Miami, FL, USA
8. Genzyme Corporation, a Sanofi Company, Framingham, MA, USA
9. Ann & Robert H. Lurie Children’s Hospital of Chicago, Chicago, IL, USA
10. Department of Molecular Pathology, Ohio State Wexner Medical Center, Columbus, OH, USA
11. University of California Los Angeles, Los Angeles, CA, USA
12. Departments of Neurology and Pediatrics, Johns Hopkins University, Baltimore, MD, USA
13. Generation Bio, Cambridge, MA, USA