Safety and Treatment Effects of Nusinersen in Longstanding Adult 5q-SMA Type 3 – A Prospective Observational Study-Reference-Cited by-同舟云学术

Safety and Treatment Effects of Nusinersen in Longstanding Adult 5q-SMA Type 3 – A Prospective Observational Study

Published:2019-10-31 Issue:4 Volume:6 Page:453-465
ISSN:2214-3599
Container-title:Journal of Neuromuscular Diseases
language:
Short-container-title:JND

Author:

Walter Maggie C.¹,Wenninger Stephan¹,Thiele Simone¹,Stauber Julia¹,Hiebeler Miriam¹,Greckl Eva¹,Stahl Kristina¹,Pechmann Astrid²,Lochmüller Hanns³,Kirschner Janbernd²⁴,Schoser Benedikt¹

Affiliation:

1. Friedrich-Baur-Institute, Department of Neurology, Ludwig-Maximilians-University of Munich, Munich, Germany

2. Department of Neuropediatrics and Muscle Disorders, Medical Center-University of Freiburg, Faculty of Medicine, University of Freiburg, Freiburg, Germany

3. Department of Neuropediatrics and Muscle Disorders, Medical Center-University of Freiburg, Faculty of Medicine, University of Freiburg, Freiburg, Germany; and Children’s Hospital of Eastern Ontario Research Institute; Division of Neurology, Department of Medicine, The Ottawa Hospital; and Brain and Mind Research Institute, University of Ottawa, Ottawa, Canada

4. Department of Neuropaediatrics, Rheinische Friedrich-Wilhelms-University Bonn, Bonn, Germany

Publisher

IOS Press

Subject

Clinical Neurology,Neurology

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3. Therapeutic strategies for spinal muscular atrophy: SMN and beyond;Bowerman;Dis Model Mech,2017

4. Nusinersen versus sham control in infantile-onset spinal muscular atrophy;Finkel;N Engl J Med,2017

5. Nusinersen versus sham control in later-onset spinal muscular atrophy;Mercuri;N Engl J Med,2018

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