Comments and Controversies in Oncology: The Tribulations of Trials Developing ONC201

Author:

Hansford Jordan R.1ORCID,Bouche Gauthier2,Ramaswamy Vijay345,Jabado Nada6,Fonseca Adriana7,Moloney Sam8,Gottardo Nicholas G.9,Robinson Giles W.10,Gajjar Amar10,Tinkle Christopher L.10,Fisher Paul G.11,Foreman Nicholas12,Ashley David M.13,Ziegler David S.141516,Eisenstat David D.17,Massimino Maura18,Witt Olaf19202122,Bartels Ute19,Rutkowski Stefan23,Hargrave Darren24,Fouladi Maryam25,Pfister Stefan M.19,Bouffet Eric26

Affiliation:

1. Michael Rice Centre for Hematology and Oncology, Women's and Children's Hospital; South Australia Health and Medical Research Institute; South Australia ImmunoGENomics Cancer Institute, University of Adelaide, Adelaide, Australia

2. The Anticancer Fund, Meise, Belgium

3. Developmental and Stem Cell Biology, Labatt Brain Tumor Research Centre, The Hospital for Sick Children, Toronto, ON, Canada

4. Division of Hematology/Oncology, Hospital for Sick Children, Toronto, ON, Canada

5. Departments of Medical Biophysics and Pediatrics, University of Toronto, Toronto, ON, Canada

6. Department of Pediatrics, McGill University, RI-MUHC, Montreal, QC, Canada

7. Children's National Hospital, Washington, DC

8. Children's Cancer Centre, Royal Children's Hospital; Murdoch Children's Research Institute, Melbourne, VIC, Australia

9. Department of Pediatric and Adolescent Oncology and Hematology, Perth Children's Hospital; Telethon Kid's Cancer Centre, Telethon Kid's Institute, University of Western Australia, Perth, WA, Australia

10. St Jude Children's Research Hospital, Memphis, TN

11. Stanford University, Palo Alto, CA

12. Colorado Children's Hospital, Denver, CO

13. Preston Robert Tisch Brain Tumor Centre, Duke University, Durham, NC

14. Children's Cancer Institute, Lowy Cancer Centre, UNSW Sydney, Kensington, NSW, Australia

15. School of Clinical Medicine, UNSW Medicine & Health, UNSW Sydney, Kensington, NSW, Australia

16. Kids Cancer Centre, Sydney Children's Hospital, Randwick, NSW, Australia

17. Children's Cancer Centre, Royal Children's Hospital; Murdoch Children's Research Institute; Department of Pediatrics, University of Melbourne, Melbourne, VIC, Australia

18. Pediatric Oncology Unit, Fondazione IRCCS Instituto Nazionale dei Tumori, Milan, Italy

19. Hopp Children's Cancer Centre Heidelberg (KiTZ), Heidelberg, Germany

20. Department of Pediatric Neurooncology, German Cancer Research Center (DKFZ) and German Cancer 36 Consortium (DKTK), Heidelberg, Germany

21. Department of Pediatric Oncology, Hematology & Immunology, Heidelberg University Hospital, Heidelberg, Germany

22. National Center for Tumor Diseases (NCT) Heidelberg, Heidelberg, Germany

23. University Medical Center Hamburg-Eppendorf, Hamburg, Germany

24. UCL Great Ormond Street Institute of Child Health, London, United Kingdom

25. Department of Neuro-Oncology, Nationwide Children's Hospital, Columbus, OH

26. The Hospital for Sick Children, University of Toronto, Toronto, ON, Canada

Abstract

Our international team highlights issues with efficacy reports in several studies on DMG with the new drug ONC201.

Publisher

American Society of Clinical Oncology (ASCO)

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