SPRINT: Phase II study of the MEK 1/2 inhibitor selumetinib (AZD6244, ARRY-142886) in children with neurofibromatosis type 1 (NF1) and inoperable plexiform neurofibromas (PN).

Author:

Gross Andrea M.1,Wolters Pamela2,Baldwin Andrea2,Dombi Eva3,Fisher Michael J.4,Weiss Brian D.5,Kim AeRang6,Blakeley Jaishri O'Neill7,Whitcomb Patricia2,Holmblad Marielle8,Martin Staci9,Roderick Marie Claire10,Paul Scott M.11,Therrien Janet9,Heisey Kara12,Doyle Austin13,Smith Malcolm A.14,Glod John15,Steinberg Seth M.2,Widemann Brigitte C.16

Affiliation:

1. National Institutes of Health, Bethesda, MD;

2. National Cancer Institute, Bethesda, MD;

3. Pediatric Oncology Branch, National Cancer Institute, Bethesda, MD;

4. Children's Hosp of Philadelphia, Philadelphia, PA;

5. Cincinnati Children's Hospital Medical Center, Cincinnati, OH;

6. Children's National Health System, Washington, DC;

7. Johns Hopkins University School of Medicine, Baltimore, MD;

8. Clinical Research Directorate/Clinical Monitoring Research Program, Leidos Biomedical Research, Inc., NCI, Frederick, MD;

9. Pediatric Oncology Branch, NCI, Bethesda, MD;

10. Pediatric Oncology Branch, National Institutes of Health, Bethesda, MD;

11. Rehabilitation Medicine Deparment, Clinical Center, NCI, Bethesda, MD;

12. Clinical Research Directorate/Clinical Monitoring Research Program, Leidos Biomedical Research, Inc, Frederick, MD;

13. National Cancer Institute, Rockville, MD;

14. Cancer Therapy Evaluation Program, National Cancer Institute, Washington, DC;

15. National Cancer Institute at the National Institutes of Health, Bethesda, MD;

16. Pediatric Oncology Branch, Center for Cancer Research, National Cancer Institute, National Institutes of Health, Bethesda, MD;

Publisher

American Society of Clinical Oncology (ASCO)

Subject

Cancer Research,Oncology

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