Glycomimetic-based pharmacological chaperones for lysosomal storage disorders: lessons from Gaucher, GM1-gangliosidosis and Fabry diseases-Reference-Cited by-同舟云学术

Glycomimetic-based pharmacological chaperones for lysosomal storage disorders: lessons from Gaucher, GM1-gangliosidosis and Fabry diseases

Published:2016 Issue:32 Volume:52 Page:5497-5515
ISSN:1359-7345
Container-title:Chemical Communications
language:en
Short-container-title:Chem. Commun.

Author:

Sánchez-Fernández Elena M.¹²³⁴⁵,García Fernández José M.⁶⁷⁸⁵,Mellet Carmen Ortiz¹²³⁴⁵^ORCID

Affiliation:

1. Departamento de Química Orgánica

2. Facultad de Química

3. Universidad de Sevilla

4. Sevilla

5. Spain

6. Instituto de Investigaciones Químicas (IIQ)

7. CSIC – Universidad de Sevilla

8. 41092 Sevilla

Abstract

Recent advancements and future outlook on pharmacological chaperones for lysosomal storage disorders using glycomimetics are discussed.

Funder

Seventh Framework Programme

Consejería Economía, Innovación, Ciencia y Empleo, Junta de Andalucia

Publisher

Royal Society of Chemistry (RSC)

Subject

Materials Chemistry,Metals and Alloys,Surfaces, Coatings and Films,General Chemistry,Ceramics and Composites,Electronic, Optical and Magnetic Materials,Catalysis

Link

http://pubs.rsc.org/en/content/articlepdf/2016/CC/C6CC01564F

Reference180 articles.

1. Lysosomal storage disorders: The cellular impact of lysosomal dysfunction

2. Lysosomal Storage Diseases: From Pathophysiology to Therapy

3. Sphingolipid lysosomal storage disorders

4. Glycosphingolipids-Nature, Function, and Pharmacological Modulation

5. Glyco-engineering strategies for the development of therapeutic enzymes with improved efficacy for the treatment of lysosomal storage diseases

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