Treatment of hypophosphatasia by muscle-directed expression of bone-targeted alkaline phosphatase via self-complementary AAV8 vector-Reference-Cited by-同舟云学术

Treatment of hypophosphatasia by muscle-directed expression of bone-targeted alkaline phosphatase via self-complementary AAV8 vector

Published:2016 Issue: Volume:3 Page:15059
ISSN:2329-0501
Container-title:Molecular Therapy - Methods & Clinical Development
language:en
Short-container-title:Molecular Therapy - Methods & Clinical Development

Author:

Nakamura-Takahashi Aki,Miyake Koichi,Watanabe Atsushi,Hirai Yukihiko,Iijima Osamu,Miyake Noriko,Adachi Kumi,Nitahara-Kasahara Yuko,Kinoshita Hideaki,Noguchi Taku,Abe Shinichi,Narisawa Sonoko,Millán Jose Luis,Shimada Takashi,Okada Takashi

Publisher

Elsevier BV

Subject

Genetics,Molecular Biology,Molecular Medicine

Reference44 articles.

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4. Mice lacking tissue non-specific alkaline phosphatase die from seizures due to defective metabolism of vitamin B-6;Waymire;Nat Genet,1995

5. Abnormal vitamin B6 metabolism in alkaline phosphatase knock-out mice causes multiple abnormalities, but not the impaired bone mineralization;Narisawa;J Pathol,2001

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