Efficacy of a Combined Intracerebral and Systemic Gene Delivery Approach for the Treatment of a Severe Lysosomal Storage Disorder-Reference-Cited by-同舟云学术

Efficacy of a Combined Intracerebral and Systemic Gene Delivery Approach for the Treatment of a Severe Lysosomal Storage Disorder

Published:2011-05 Issue:5 Volume:19 Page:860-869
ISSN:1525-0016
Container-title:Molecular Therapy
language:en
Short-container-title:Molecular Therapy

Author:

Spampanato Carmine,De Leonibus Elvira,Dama Paola,Gargiulo Annagiusi,Fraldi Alessandro,Sorrentino Nicolina Cristina,Russo Fabio,Nusco Edoardo,Auricchio Alberto,Surace Enrico M,Ballabio Andrea

Publisher

Elsevier BV

Subject

Drug Discovery,Pharmacology,Genetics,Molecular Biology,Molecular Medicine

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