Gene Correction by Homologous Recombination With Zinc Finger Nucleases in Primary Cells From a Mouse Model of a Generic Recessive Genetic Disease
Author:
Publisher
Elsevier BV
Subject
Drug Discovery,Pharmacology,Genetics,Molecular Biology,Molecular Medicine
Reference50 articles.
1. Sustained correction of X-linked severe combined immunodeficiency by ex vivo gene therapy;Hacein-Bey-Abina;N Engl J Med,2002
2. Gene therapy for immunodeficiency due to adenosine deaminase deficiency;Aiuti;N Engl J Med,2009
3. Effect of gene therapy on visual function in Leber's congenital amaurosis;Bainbridge;N Engl J Med,2008
4. Age-dependent effects of RPE65 gene therapy for Leber's congenital amaurosis: a phase 1 dose-escalation trial;Maguire;Lancet,2009
5. Hematopoietic stem cell gene therapy with a lentiviral vector in X-linked adrenoleukodystrophy;Cartier;Science,2009
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