Proteasome Inhibitors Enhance Gene Delivery by AAV Virus Vectors Expressing Large Genomes in Hemophilia Mouse and Dog Models: A Strategy for Broad Clinical Application-Reference-Cited by-同舟云学术

Proteasome Inhibitors Enhance Gene Delivery by AAV Virus Vectors Expressing Large Genomes in Hemophilia Mouse and Dog Models: A Strategy for Broad Clinical Application

Published:2010-11 Issue:11 Volume:18 Page:1907-1916
ISSN:1525-0016
Container-title:Molecular Therapy
language:en
Short-container-title:Molecular Therapy

Author:

Monahan Paul E,Lothrop Clinton D,Sun Junjiang,Hirsch Matthew L,Kafri Tal,Kantor Boris,Sarkar Rita,Tillson D Michael,Elia Joseph R,Samulski R Jude

Publisher

Elsevier BV

Subject

Drug Discovery,Pharmacology,Genetics,Molecular Biology,Molecular Medicine

Reference50 articles.

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5. Complete correction of hemophilia A with adeno-associated viral vectors containing a full-size expression cassette;Lu;Hum Gene Ther,2008

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