Neonatal Gene Therapy of Glycogen Storage Disease Type Ia Using a Feline Immunodeficiency Virus

Neonatal Gene Therapy of Glycogen Storage Disease Type Ia Using a Feline Immunodeficiency Virus–based Vector

Published:2010-09 Issue:9 Volume:18 Page:1592-1598
ISSN:1525-0016
Container-title:Molecular Therapy
language:en
Short-container-title:Molecular Therapy

Author:

Grinshpun Albert,Condiotti Reba,N Waddington Simon,Peer Michael,Zeig Eli,Peretz Sima,Simerzin Alina,Chou Janice,Pann Chi-Jiunn,Giladi Hilla,Galun Eithan

Publisher

Elsevier BV

Subject

Drug Discovery,Pharmacology,Genetics,Molecular Biology,Molecular Medicine

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