Safe, Efficient, and Reproducible Gene Therapy of the Brain in the Dog Models of Sanfilippo and Hurler Syndromes-Reference-Cited by-同舟云学术

Safe, Efficient, and Reproducible Gene Therapy of the Brain in the Dog Models of Sanfilippo and Hurler Syndromes

Published:2011-02 Issue:2 Volume:19 Page:251-259
ISSN:1525-0016
Container-title:Molecular Therapy
language:en
Short-container-title:Molecular Therapy

Author:

Ellinwood N Matthew,Ausseil Jérôme,Desmaris Nathalie,Bigou Stéphanie,Liu Song,Jens Jackie K,Snella Elizabeth M,Mohammed Eman EA,Thomson Christopher B,Raoul Sylvie,Joussemet Béatrice,Roux Françoise,Chérel Yan,Lajat Yaouen,Piraud Monique,Benchaouir Rachid,Hermening Stephan,Petry Harald,Froissart Roseline,Tardieu Marc,Ciron Carine,Moullier Philippe,Parkes Jennifer,Kline Karen L,Maire Irène,Vanier Marie-Thérèse,Heard Jean-Michel,Colle Marie-Anne

Publisher

Elsevier BV

Subject

Drug Discovery,Pharmacology,Genetics,Molecular Biology,Molecular Medicine

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