A MicroRNA-regulated and GP64-pseudotyped Lentiviral Vector Mediates Stable Expression of FVIII in a Murine Model of Hemophilia A-Reference-Cited by-同舟云学术

A MicroRNA-regulated and GP64-pseudotyped Lentiviral Vector Mediates Stable Expression of FVIII in a Murine Model of Hemophilia A

Published:2011-04 Issue:4 Volume:19 Page:723-730
ISSN:1525-0016
Container-title:Molecular Therapy
language:en
Short-container-title:Molecular Therapy

Author:

Matsui Hideto,Hegadorn Carol,Ozelo Margareth,Burnett Erin,Tuttle Angie,Labelle Andrea,McCray Paul B,Naldini Luigi,Brown Brian,Hough Christine,Lillicrap David

Publisher

Elsevier BV

Subject

Drug Discovery,Pharmacology,Genetics,Molecular Biology,Molecular Medicine

Reference48 articles.

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4. Non-genetic risk factors and the development of inhibitors in haemophilia: a comprehensive review and consensus report;Astermark;Haemophilia,2010

5. Antioxidants reduce endoplasmic reticulum stress and improve protein secretion;Malhotra;Proc Natl Acad Sci USA,2008

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