AAV-mediated gene transfer for the treatment of hemophilia B: problems and prospects
Author:
Publisher
Springer Science and Business Media LLC
Subject
Genetics,Molecular Biology,Molecular Medicine
Link
http://www.nature.com/articles/gt200871.pdf
Reference35 articles.
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3. Schwarzwaelder K, Howe SJ, Schmidt M, Brugman MH, Deichmann A, Glimm H et al. Gammaretrovirus-mediated correction of SCID-X1 is associated with skewed vector integration site distribution in vivo. J Clin Invest 2007; 117: 2241–2249.
4. Lofqvist T, Nilsson IM, Berntorp E, Pettersson H . Haemophilia prophylaxis in young patients—a long-term follow-up. J Intern Med 1997; 241: 395–400.
5. Bray GL, Luban NL . Hemophilia presenting with intracranial hemorrhage. An approach to the infant with intracranial bleeding and coagulopathy. Am J Dis Child 1987; 141: 1215–1217.
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