Successful Regional Delivery and Long-term Expression of a Dystrophin Gene in Canine Muscular Dystrophy: A Preclinical Model for Human Therapies-Reference-Cited by-同舟云学术

Successful Regional Delivery and Long-term Expression of a Dystrophin Gene in Canine Muscular Dystrophy: A Preclinical Model for Human Therapies

Published:2012-08 Issue:8 Volume:20 Page:1501-1507
ISSN:1525-0016
Container-title:Molecular Therapy
language:en
Short-container-title:Molecular Therapy

Author:

Wang Zejing,Storb Rainer,Halbert Christine L,Banks Glen B.,Butts Tiffany M.,Finn Eric E.,Allen James M.,Miller A. Dusty,Chamberlain Jeffrey S.,Tapscott Stephen J.

Publisher

Elsevier BV

Subject

Drug Discovery,Pharmacology,Genetics,Molecular Biology,Molecular Medicine

Reference49 articles.

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4. Gene therapy in large animal models of muscular dystrophy;Wang;ILAR J,2009

5. Systemic delivery of genes to striated muscles using adeno-associated viral vectors;Gregorevic;Nat Med,2004

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