Improved Survival and Reduced Phenotypic Severity Following AAV9/MECP2 Gene Transfer to Neonatal and Juvenile Male Mecp2 Knockout Mice-Reference-Cited by-同舟云学术

Improved Survival and Reduced Phenotypic Severity Following AAV9/MECP2 Gene Transfer to Neonatal and Juvenile Male Mecp2 Knockout Mice

Published:2013-01 Issue:1 Volume:21 Page:18-30
ISSN:1525-0016
Container-title:Molecular Therapy
language:en
Short-container-title:Molecular Therapy

Author:

Gadalla Kamal KE,Bailey Mark ES,Spike Rosemary C,Ross Paul D,Woodard Kenton T,Kalburgi Sahana Nagabhushan,Bachaboina Lavanya,Deng Jie V,West Anne E,Samulski R Jude,Gray Steven J,Cobb Stuart R

Publisher

Elsevier BV

Subject

Drug Discovery,Pharmacology,Genetics,Molecular Biology,Molecular Medicine

Reference49 articles.

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4. Deficiency of methyl-CpG binding protein-2 in CNS neurons results in a Rett-like phenotype in mice;Chen;Nat Genet,2001

5. Partial rescue of MeCP2 deficiency by postnatal activation of MeCP2;Giacometti;Proc Natl Acad Sci USA,2007

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