Challenges in Vector and Trial Design Using Retroviral Vectors for Long-Term Gene Correction in Hematopoietic Stem Cell Gene Therapy-Reference-Cited by-同舟云学术

Challenges in Vector and Trial Design Using Retroviral Vectors for Long-Term Gene Correction in Hematopoietic Stem Cell Gene Therapy

Published:2012-06 Issue:6 Volume:20 Page:1084-1094
ISSN:1525-0016
Container-title:Molecular Therapy
language:en
Short-container-title:Molecular Therapy

Author:

Corrigan-Curay Jacqueline,Cohen-Haguenauer Odile,O'Reilly Marina,Ross Susan R.,Fan Hung,Rosenberg Naomi,Somia Nikunj,King Nancy,Friedmann Theodore,Dunbar Cynthia,Aiuti Alessandro,Naldini Luigi,Baum Christopher,von Kalle Christof,Kiem Hans-Peter,Montini Eugenio,Bushman Frederic,Sorrentino Brian P,Carrondo Manuel,Malech Harry,Gahrton Gösta,Shapiro Robyn,Wolff Linda,Rosenthal Eugene,Jambou Robert,Zaia John,Kohn Donald B

Publisher

Elsevier BV

Subject

Drug Discovery,Pharmacology,Genetics,Molecular Biology,Molecular Medicine

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5. Correction of X-linked chronic granulomatous disease by gene therapy, augmented by insertional activation of MDS1-EVI1, PRDM16 or SETBP1;Ott;Nat Med,2006

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