Gene Transfer Corrects Acute GM2 Gangliosidosis—Potential Therapeutic Contribution of Perivascular Enzyme Flow-Reference-Cited by-同舟云学术

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Gene Transfer Corrects Acute GM2 Gangliosidosis—Potential Therapeutic Contribution of Perivascular Enzyme Flow

Published:2012-08 Issue:8 Volume:20 Page:1489-1500
ISSN:1525-0016
Container-title:Molecular Therapy
language:en
Short-container-title:Molecular Therapy

Author:

Cachón-González M Begoña,Wang Susan Z,McNair Rosamund,Bradley Josephine,Lunn David,Ziegler Robin,Cheng Seng H,Cox Timothy M

Publisher

Elsevier BV

Subject

Drug Discovery,Pharmacology,Genetics,Molecular Biology,Molecular Medicine

Reference49 articles.

1. The clinical spectrum of hexosaminidase deficiency diseases;Johnson;Neurology,1981

2. Demonstration of an alteration of ganglioside metabolism in Tay-Sachs disease;Kolodny;Biochem Biophys Res Commun,1969

3. Tay-Sachs disease: generalized absence of a beta-D-N-acetylhexosaminidase component;Okada;Science,1969

4. Variation of beta-N-acetylhexosaminidase-pattern in Tay-Sachs disease;Sandhoff;FEBS Lett,1969

5. Purification and characterization of an activator protein for the degradation of glycolipids GM2 and GA2 by hexosaminidase A;Conzelmann;Hoppe-Seyler's Z Physiol Chem,1979

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