Correction of Murine Rag2 Severe Combined Immunodeficiency by Lentiviral Gene Therapy Using a Codon-optimized RAG2 Therapeutic Transgene-Reference-Cited by-同舟云学术

Correction of Murine Rag2 Severe Combined Immunodeficiency by Lentiviral Gene Therapy Using a Codon-optimized RAG2 Therapeutic Transgene

Published:2012-10 Issue:10 Volume:20 Page:1968-1980
ISSN:1525-0016
Container-title:Molecular Therapy
language:en
Short-container-title:Molecular Therapy

Author:

van Til Niek P,de Boer Helen,Mashamba Nomusa,Wabik Agnieszka,Huston Marshall,Visser Trudi P,Fontana Elena,Poliani Pietro Luigi,Cassani Barbara,Zhang Fang,Thrasher Adrian J,Villa Anna,Wagemaker Gerard

Publisher

Elsevier BV

Subject

Drug Discovery,Pharmacology,Genetics,Molecular Biology,Molecular Medicine

Reference47 articles.

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