Muscle Function Recovery in Golden Retriever Muscular Dystrophy After AAV1-U7 Exon Skipping-Reference-Cited by-同舟云学术

Muscle Function Recovery in Golden Retriever Muscular Dystrophy After AAV1-U7 Exon Skipping

Published:2012-11 Issue:11 Volume:20 Page:2120-2133
ISSN:1525-0016
Container-title:Molecular Therapy
language:en
Short-container-title:Molecular Therapy

Author:

Vulin Adeline,Barthélémy Inès,Goyenvalle Aurélie,Thibaud Jean-Laurent,Beley Cyriaque,Griffith Graziella,Benchaouir Rachid,le Hir Maëva,Unterfinger Yves,Lorain Stéphanie,Dreyfus Patrick,Voit Thomas,Carlier Pierre,Blot Stéphane,Garcia Luis

Publisher

Elsevier BV

Subject

Drug Discovery,Pharmacology,Genetics,Molecular Biology,Molecular Medicine

Reference52 articles.

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2. Transcription of the dystrophin gene in human muscle and non-muscle tissue;Chelly;Nature,1988

3. Duchenne muscular dystrophy: deficiency of dystrophin at the muscle cell surface;Bonilla;Cell,1988

4. Dystrophin protects the sarcolemma from stresses developed during muscle contraction;Petrof;Proc Natl Acad Sci USA,1993

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