A Gene Gun-mediated Nonviral RNA trans-splicing Strategy for Col7a1 Repair-Reference-Cited by-同舟云学术

A Gene Gun-mediated Nonviral RNA trans-splicing Strategy for Col7a1 Repair

Published:2016 Issue: Volume:5 Page:e287
ISSN:2162-2531
Container-title:Molecular Therapy - Nucleic Acids
language:en
Short-container-title:Molecular Therapy - Nucleic Acids

Author:

Peking Patricia,Koller Ulrich,Hainzl Stefan,Kitzmueller Sophie,Kocher Thomas,Mayr Elisabeth,Nyström Alexander,Lener Thomas,Reichelt Julia,Bauer Johann W,Murauer Eva M

Publisher

Elsevier BV

Subject

Drug Discovery,Molecular Medicine

Reference35 articles.

1. Repair of CFTR mRNA by spliceosome-mediated RNA trans-splicing;Mansfield;Gene Ther,2000

2. K14 mRNA reprogramming for dominant epidermolysis bullosa simplex;Wally;Hum Mol Genet,2010

3. Functional correction of type VII collagen expression in dystrophic epidermolysis bullosa;Murauer;J Invest Dermatol,2011

4. Repair of Mybpc3 mRNA by 5′-trans-splicing in a mouse model of hypertrophic cardiomyopathy;Mearini;Mol Ther Nucleic Acids,2013

5. Development of spliceosome-mediated RNA trans-splicing (SMaRT) for the correction of inherited skin diseases;Dallinger;Exp Dermatol,2003

Cited by 36 articles. 订阅此论文施引文献订阅此论文施引文献，注册后可以免费订阅5篇论文的施引文献，订阅后可以查看论文全部施引文献

1. RNA exon editing: Splicing the way to treat human diseases;Molecular Therapy - Nucleic Acids;2024-09

2. Emerging DNA & RNA editing strategies for the treatment of epidermolysis bullosa;Journal of Dermatological Treatment;2024-08-18

3. Biolistic delivery of liposomes protected in metal-organic frameworks;Proceedings of the National Academy of Sciences;2023-03-06

4. COL7A1 Editing via RNA Trans-Splicing in RDEB-Derived Skin Equivalents;International Journal of Molecular Sciences;2023-02-22

5. Stairways to Advanced Therapies for Epidermolysis Bullosa;Cold Spring Harbor Perspectives in Biology;2022-09-27