Targeted Exon Skipping to Correct Exon Duplications in the Dystrophin Gene
Author:
Publisher
Elsevier BV
Subject
Drug Discovery,Molecular Medicine
Reference31 articles.
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3. Duchenne muscular dystrophy: pathogenetic aspects and genetic prevention;Moser;Hum Genet,1984
4. The complete sequence of dystrophin predicts a rod-shaped cytoskeletal protein;Koenig;Cell,1988
5. An explanation for the phenotypic differences between patients bearing partial deletions of the DMD locus;Monaco;Genomics,1988
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