Quantification of lentiviral vector copy numbers in individual hematopoietic colony-forming cells shows vector dose-dependent effects on the frequency and level of transduction-Reference-Cited by-同舟云学术

Quantification of lentiviral vector copy numbers in individual hematopoietic colony-forming cells shows vector dose-dependent effects on the frequency and level of transduction

Published:2010-12-16 Issue:5 Volume:18 Page:479-487
ISSN:0969-7128
Container-title:Gene Therapy
language:en
Short-container-title:Gene Ther

Author:

Charrier S,Ferrand M,Zerbato M,Précigout G,Viornery A,Bucher-Laurent S,Benkhelifa-Ziyyat S,Merten O W,Perea J,Galy A

Publisher

Springer Science and Business Media LLC

Subject

Genetics,Molecular Biology,Molecular Medicine

Link

http://www.nature.com/articles/gt2010163.pdf

Reference22 articles.

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2. Piacibello W, Bruno S, Sanavio F, Droetto S, Gunetti M, Ailles L et al. Lentiviral gene transfer and ex vivo expansion of human primitive stem cells capable of primary, secondary, and tertiary multilineage repopulation in NOD/SCID mice. Nonobese diabetic/severe combined immunodeficient. Blood 2002; 100: 4391–4400.

3. Enssle J, Trobridge GD, Keyser KA, Ironside C, Beard BC, Kiem HP . Stable marking and transgene expression without progression to monoclonality in canine long-term hematopoietic repopulating cells transduced with lentiviral vectors. Hum Gene Ther 2010; 21: 397–403.

4. Woods NB, Fahlman C, Mikkola H, Hamaguchi I, Olsson K, Zufferey R et al. Lentiviral gene transfer into primary and secondary NOD/SCID repopulating cells. Blood 2000; 96: 3725–3733.

5. Cartier N, Hacein-Bey-Abina S, Bartholomae CC, Veres G, Schmidt M, Kutschera I et al. Hematopoietic stem cell gene therapy with a lentiviral vector in X-linked adrenoleukodystrophy. Science 2009; 326: 818–823.

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