Concurrent progress of reprogramming and gene correction to overcome therapeutic limitation of mutant ALK2-iPSC
Author:
Publisher
Springer Science and Business Media LLC
Subject
Clinical Biochemistry,Molecular Biology,Molecular Medicine,Biochemistry
Link
http://www.nature.com/articles/emm201643.pdf
Reference39 articles.
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3. Filareto A, Parker S, Darabi R, Borges L, Iacovino M, Schaaf T et al. An ex vivo gene therapy approach to treat muscular dystrophy using inducible pluripotent stem cells. Nat Commun 2013; 4: 1549.
4. Li HL, Fujimoto N, Sasakawa N, Shirai S, Ohkame T, Sakuma T et al. Precise correction of the dystrophin gene in duchenne muscular dystrophy patient induced pluripotent stem cells by TALEN and CRISPR-Cas9. Stem Cell Reports 2015; 4: 143–154.
5. Fairchild PJ . The challenge of immunogenicity in the quest for induced pluripotency. Nat Rev Immunol 2010; 10: 868–875.
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