Stable Human FIX Expression After 0.9G Intrauterine Gene Transfer of Self-complementary Adeno-associated Viral Vector 5 and 8 in Macaques-Reference-Cited by-同舟云学术

Stable Human FIX Expression After 0.9G Intrauterine Gene Transfer of Self-complementary Adeno-associated Viral Vector 5 and 8 in Macaques

Published:2011-11 Issue:11 Volume:19 Page:1950-1960
ISSN:1525-0016
Container-title:Molecular Therapy
language:en
Short-container-title:Molecular Therapy

Author:

Mattar Citra NZ,Nathwani Amit C,Waddington Simon N,Dighe Niraja,Kaeppel Christine,Nowrouzi Ali,Mcintosh Jenny,Johana Nuryanti B,Ogden Bryan,Fisk Nicholas M,Davidoff Andrew M,David Anna,Peebles Donald,Valentine Marcus B,Appelt Jens-Uwe,von Kalle Christof,Schmidt Manfred,Biswas Arijit,Choolani Mahesh,Chan Jerry KY

Publisher

Elsevier BV

Subject

Drug Discovery,Pharmacology,Genetics,Molecular Biology,Molecular Medicine

Reference49 articles.

1. Prenatal stem cell transplantation and gene therapy;Santore;Clin Perinatol,2009

2. Correction of hemophilia B in canine and murine models using recombinant adeno-associated viral vectors;Snyder;Nat Med,1999

3. Immune responses to AAV in clinical trials;Mingozzi;Curr Gene Ther,2007

4. Ontogeny of CD4+CD25+ regulatory/suppressor T cells in human fetuses;Darrasse-Jèze;Blood,2005

5. Gestational age of recipient determines pattern and level of transgene expression following in utero retroviral gene transfer;Porada;Mol Ther,2005

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