Long-term Restoration of Cardiac Dystrophin Expression in Golden Retriever Muscular Dystrophy Following rAAV6-mediated Exon Skipping-Reference-Cited by-同舟云学术

Long-term Restoration of Cardiac Dystrophin Expression in Golden Retriever Muscular Dystrophy Following rAAV6-mediated Exon Skipping

Published:2012-03 Issue:3 Volume:20 Page:580-589
ISSN:1525-0016
Container-title:Molecular Therapy
language:en
Short-container-title:Molecular Therapy

Author:

Bish Lawrence T,Sleeper Meg M,Forbes Sean C,Wang Bingjing,Reynolds Caryn,Singletary Gretchen E,Trafny Dennis,Morine Kevin J,Sanmiguel Julio,Cecchini Sylvain,Virag Tamas,Vulin Adeline,Beley Cyriaque,Bogan Janet,Wilson James M,Vandenborne Krista,Kornegay Joe N,Walter Glenn A,Kotin Robert M,Garcia Luis,Sweeney H Lee

Publisher

Elsevier BV

Subject

Drug Discovery,Pharmacology,Genetics,Molecular Biology,Molecular Medicine

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