ATP7A Gene Addition to the Choroid Plexus Results in Long-term Rescue of the Lethal Copper Transport Defect in a Menkes Disease Mouse Model-Reference-Cited by-同舟云学术

ATP7A Gene Addition to the Choroid Plexus Results in Long-term Rescue of the Lethal Copper Transport Defect in a Menkes Disease Mouse Model

Published:2011-12 Issue:12 Volume:19 Page:2114-2123
ISSN:1525-0016
Container-title:Molecular Therapy
language:en
Short-container-title:Molecular Therapy

Author:

Donsante Anthony,Yi Ling,Zerfas Patricia M,Brinster Lauren R,Sullivan Patricia,Goldstein David S,Prohaska Joseph,Centeno Jose A,Rushing Elisabeth,Kaler Stephen G

Publisher

Elsevier BV

Subject

Drug Discovery,Pharmacology,Genetics,Molecular Biology,Molecular Medicine

Reference50 articles.

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2. Isolation of a candidate gene for Menkes disease and evidence that it encodes a copper-transporting ATPase;Vulpe;Nat Genet,1993

3. Isolation of a candidate gene for Menkes disease that encodes a potential heavy metal binding protein;Chelly;Nat Genet,1993

4. Isolation of a partial candidate gene for Menkes disease by positional cloning;Mercer;Nat Genet,1993

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