Pip5 Transduction Peptides Direct High Efficiency Oligonucleotide-mediated Dystrophin Exon Skipping in Heart and Phenotypic Correction in mdx Mice-Reference-Cited by-同舟云学术

Pip5 Transduction Peptides Direct High Efficiency Oligonucleotide-mediated Dystrophin Exon Skipping in Heart and Phenotypic Correction in mdx Mice

Published:2011-07 Issue:7 Volume:19 Page:1295-1303
ISSN:1525-0016
Container-title:Molecular Therapy
language:en
Short-container-title:Molecular Therapy

Author:

Yin HaiFang,Saleh Amer F,Betts Corinne,Camelliti Patrizia,Seow Yiqi,Ashraf Shirin,Arzumanov Andrey,Hammond Suzan,Merritt Thomas,Gait Michael J,Wood Matthew JA

Publisher

Elsevier BV

Subject

Drug Discovery,Pharmacology,Genetics,Molecular Biology,Molecular Medicine

Reference32 articles.

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4. Therapeutic antisense-induced exon skipping in cultured muscle cells from six different DMD patients;Aartsma-Rus;Hum Mol Genet,2003

5. Therapeutic modulation of DMD splicing by blocking exonic splicing enhancer sites with antisense oligonucleotides;Aartsma-Rus;Ann N Y Acad Sci,2006

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