In vivo CRISPR editing with no detectable genome-wide off-target mutations-Reference-Cited by-同舟云学术

In vivo CRISPR editing with no detectable genome-wide off-target mutations

Published:2018-09 Issue:7723 Volume:561 Page:416-419
ISSN:0028-0836
Container-title:Nature
language:en
Short-container-title:Nature

Author:

Akcakaya Pinar,Bobbin Maggie L.,Guo Jimmy A.,Malagon-Lopez Jose,Clement Kendell,Garcia Sara P.,Fellows Mick D.,Porritt Michelle J.,Firth Mike A.,Carreras Alba,Baccega Tania,Seeliger Frank,Bjursell Mikael,Tsai Shengdar Q.,Nguyen Nhu T.,Nitsch Roberto,Mayr Lorenz M.,Pinello Luca,Bohlooly-Y Mohammad,Aryee Martin J.,Maresca Marcello,Joung J. Keith

Publisher

Springer Science and Business Media LLC

Subject

Multidisciplinary

Link

http://www.nature.com/articles/s41586-018-0500-9.pdf

Reference21 articles.

1. Musunuru, K. The hope and hype of CRISPR-Cas9 genome editing: a review. JAMA Cardiol. 2, 914–919 (2017).

2. Fellmann, C., Gowen, B. G., Lin, P. C., Doudna, J. A. & Corn, J. E. Cornerstones of CRISPR–Cas in drug discovery and therapy. Nat. Rev. Drug Discov. 16, 89–100 (2017).

3. Komor, A. C., Badran, A. H. & Liu, D. R. CRISPR-based technologies for the manipulation of eukaryotic genomes. Cell 168, 20–36 (2017).

4. Koo, T. & Kim, J. S. Therapeutic applications of CRISPR RNA-guided genome editing. Brief. Funct. Genomics 16, 38–45 (2017).

5. Cornu, T. I., Mussolino, C. & Cathomen, T. Refining strategies to translate genome editing to the clinic. Nat. Med. 23, 415–423 (2017).

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