The Combination of CRISPR/Cas9 and iPSC Technologies in the Gene Therapy of Human β-thalassemia in Mice
Author:
Publisher
Springer Science and Business Media LLC
Subject
Multidisciplinary
Link
http://www.nature.com/articles/srep32463.pdf
Reference39 articles.
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3. Galanello, R. & Origa, R. Beta-thalassemia. Orphanet journal of rare diseases 5, 11, 10.1186/1750-1172-5-11 (2010).
4. Xu, X. M. et al. The prevalence and spectrum of alpha and beta thalassaemia in Guangdong Province: implications for the future health burden and population screening. Journal of clinical pathology 57, 517–522 (2004).
5. Ou, Z., Li, Q., Liu, W. & Sun, X. Elevated hemoglobin A2 as a marker for beta-thalassemia trait in pregnant women. The Tohoku journal of experimental medicine 223, 223–226 (2011).
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