Thiotepa-based reduced toxicity conditioning in combination with post-transplant cyclophosphamide and mTOR inhibitor for heavily transfused acquired severe aplastic anemia in children and young adults: encouraging outcomes of a pilot study
Author:
Publisher
Springer Science and Business Media LLC
Subject
Transplantation,Hematology
Link
https://www.nature.com/articles/s41409-022-01876-3.pdf
Reference31 articles.
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2. Barone A, Lucarelli A, Onofrillo D, Verzegnassi F, Bonanomi S, Cesaro S, et al. Diagnosis and management of acquired aplastic anemia in childhood. Guidelines from the Marrow Failure Study Group of the Pediatric Haemato-Oncology Italian Association (AIEOP). Blood Cells Mol Dis. 2015;55:40–7.
3. Young NS, editor. Epidemiology of aplastic anemia. In: Bone marrow failure syndromes. 1st ed. Philadelphia: WB Saunders Company; 1996. p. 1–46.
4. Peffault de Latour R. Transplantation for bone marrow failure: current issues. Hematology. 2016;2016:90–8.
5. Dufour C, Veys P, Carraro E, Bhatnagar N, Pillon M, Samarasinghe S, et al. Similar outcome of upfront-unrelated and matched sibling stem cell transplantation in idiopathic paediatric aplastic anaemia. A study on behalf of the UK Paediatric BMT Working Party, Paediatric Diseases Working Party and Severe Aplastic Anaemia Working Party of EBMT. Br J Haematol. 2015;171:585–94.
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