Expression of human β–hexosaminidase α–subunit gene (the gene defect of Tay–Sachs disease) in mouse brains upon engraftment of transduced progenitor cells

Author:

Lacorazza H. Daniel,Flax Jonathan D.,Snyder Evan Y.,Jendoubi Moncef

Publisher

Springer Science and Business Media LLC

Subject

General Biochemistry, Genetics and Molecular Biology,General Medicine

Cited by 204 articles. 订阅此论文施引文献 订阅此论文施引文献,注册后可以免费订阅5篇论文的施引文献,订阅后可以查看论文全部施引文献

1. Increasing β-hexosaminidase A activity using genetically modified mesenchymal stem cells;Neural Regeneration Research;2024-01

2. Fetal gene therapy;Journal of Inherited Metabolic Disease;2023-08-07

3. Strategies to combat Tay-Sachs disease;Drug Delivery Systems for Metabolic Disorders;2022

4. Stem Cell Research Tools in Human Metabolic Disorders: An Overview;Cells;2021-10-07

5. Sphingolipid lysosomal storage diseases: from bench to bedside;Lipids in Health and Disease;2021-05-03

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