Safety and efficacy of N-acetylmannosamine (ManNAc) in patients with GNE myopathy: an open-label phase 2 study
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Published:2021-11
Issue:11
Volume:23
Page:2067-2075
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ISSN:1098-3600
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Container-title:Genetics in Medicine
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language:en
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Short-container-title:Genetics in Medicine
Author:
Carrillo NuriaORCID,
Malicdan May C.,
Leoyklang Petcharat,
Shrader Joseph A.,
Joe Galen,
Slota Christina,
Perreault John,
Heiss John D.,
Class Bradley,
Liu Chia-Ying,
Bradley Kennan,
Jodarski Colleen,
Ciccone Carla,
Driscoll Claire,
Parks Rebecca,
Van Wart Scott,
Bayman Levent,
Coffey Christopher S.,
Quintana Melanie,
Berry Scott M.,
Huizing Marjan,
Gahl William A.
Subject
Genetics (clinical)
Cited by
29 articles.
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