Progress and Prospects: Gene Therapy Clinical Trials (Part 2)
Author:
Publisher
Springer Science and Business Media LLC
Subject
Genetics,Molecular Biology,Molecular Medicine
Link
http://www.nature.com/articles/3303033.pdf
Reference47 articles.
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3. Harper SQ, Staber PD, He X, Eliason SL, Martins IH, Mao Q et al. RNA interference improves motor and neuropathological abnormalities in a Huntington's disease mouse model. Proc Natl Acad Sci USA 2005; 102: 5820–5825.
4. Rodriguez-Lebron E, Denovan-Wright EM, Nash K, Lewin AS, Mandel RJ . Intrastriatal rAAV-mediated delivery of anti-huntingtin shRNAs induces partial reversal of disease progression in R6/1 Huntington's disease transgenic mice. Mol Ther 2005; 12: 618–633.
5. Mittoux V, Ouary S, Monville C, Lisovoski F, Poyot T, Conde F et al. Corticostriatopallidal neuroprotection by adenovirus-mediated ciliary neurotrophic factor gene transfer in a rat model of progressive striatal degeneration. J Neurosci 2002; 22: 4478–4486.
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