Major role of local immune responses in antibody formation to factor IX in AAV gene transfer-Reference-Cited by-同舟云学术

Major role of local immune responses in antibody formation to factor IX in AAV gene transfer

Published:2005-05-12 Issue:19 Volume:12 Page:1453-1464
ISSN:0969-7128
Container-title:Gene Therapy
language:en
Short-container-title:Gene Ther

Author:

Wang L,Cao O,Swalm B,Dobrzynski E,Mingozzi F,Herzog R W

Publisher

Springer Science and Business Media LLC

Subject

Genetics,Molecular Biology,Molecular Medicine

Link

http://www.nature.com/articles/3302539.pdf

Reference35 articles.

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2. High KA . Gene transfer as an approach to treating hemophilia. Semin Thromb Hemost 2003; 29: 107–120.

3. Mount JD et al. Sustained phenotypic correction of hemophilia B dogs with a factor IX null mutation by liver-directed gene therapy. Blood 2002; 99: 2670–2676.

4. Herzog RW et al. Long-term correction of canine hemophilia B by gene transfer of blood coagulation factor IX mediated by adeno-associated viral vector. Nat Med 1999; 5: 56–63.

5. Manno CS et al. AAV-mediated factor IX gene transfer to skeletal muscle in patients with severe hemophilia B. Blood 2003; 101: 2963–2972.

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